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Pompe Disease Pipeline Drugs and Companies Insight Report (2022): Analysis of Clinical Trials, Therapies, Mechanism of Action, Route of Administration, and Developments

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Pompe Disease Pipeline Drugs and Companies Insight Report (2022): Analysis of Clinical Trials, Therapies, Mechanism of Action, Route of Administration, and Developments

November 14
23:09 2022
Pompe Disease Pipeline Drugs and Companies Insight Report (2022): Analysis of Clinical Trials, Therapies, Mechanism of Action, Route of Administration, and Developments
Pompe Disease pipeline constitutes 15+ key companies continuously working towards developing 20+ Pompe Disease treatment therapies, analysis of Clinical Trials, Therapies, Mechanism of Action, Route of Administration, and Developments analyzes DelveInsight.

Pompe Disease Overview

Pompe disease belongs to the ‘lysosomal storage disorders’ (LSDs) group of diseases. Within the cells, lysosomes are tiny compartments where all sorts of substances are recycled. By the action of digestive enzymes, the compounds are degraded. There are currently more than 50 different LSDs that are considered to be caused by the deficiency of one of these enzymes

“Pompe Disease Pipeline Insight, 2022″ report by DelveInsight outlines comprehensive insights into the present clinical development scenario and growth prospects across the Pompe Disease Market. 

The Pompe Disease Pipeline report embraces in-depth commercial and clinical assessment of the pipeline products from the pre-clinical developmental phase to the marketed phase. The report also covers a detailed description of the drug, including the mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, collaborations, mergers acquisition, funding, designations, and other product-related details. 

Some of the key takeaways from the Pompe Disease Pipeline Report: https://www.delveinsight.com/report-store/pompe-disease-pipeline-insight?utm_source=abnewswire&utm_medium=pressrelease&utm_campaign=gpr

  • Companies across the globe are diligently working toward developing novel Pompe Disease treatment therapies with a considerable amount of success over the years. Pompe Disease Key players such as – M6P Therapeutics, Entrada Therapeutics, Maze Therapeutics, Astellas Gene Therapies, Asklepios Biopharmaceutical, Spark Therapeutic, Amicus Therapeutics, and others, are developing therapies for the Pompe Disease treatment 
  • Pompe Disease Emerging therapies such as – M 021, GYS1 Knockdown Oligonucleotide, MZE 001, AT845, AAV2/8LSPhGAA, SPK-3006, Cipaglucosidase alfa, and others are expected to have a significant impact on the Pompe Disease market in the coming years.   
  • In February 2020, Amicus Therapeutics initiated an open-label study of the safety, pharmacokinetics, efficacy, pharmacodynamics, and immunogenicity of ATB200/AT2221 in pediatric subjects aged 0 to < 18 years with Pompe Disease. The trial is currently recruiting participants and is expected to be completed by June 2026
  • In December 2021, Amicus Therapeutics (announced that the European Medicines Agency (EMA) validated the Marketing Authorization Applications (MAA) for AT-GAA, the Company’s investigational two-component therapy for the treatment of Pompe disease 

 

Pompe Disease Pipeline Therapeutics Assessment

  • Pompe Disease Assessment by Product Type
  • Pompe Disease By Stage and Product Type
  • Pompe Disease Assessment by Route of Administration
  • Pompe Disease By Stage and Route of Administration
  • Pompe Disease Assessment by Molecule Type
  • Pompe Disease by Stage and Molecule Type

 

DelveInsight’s Pompe Disease Report covers around 20+ products under different phases of clinical development like

  • Late-stage products (Phase III)
  • Mid-stage products (Phase II)
  • Early-stage product (Phase I)
  • Pre-clinical and Discovery stage candidates
  • Discontinued & Inactive candidates
  • Route of Administration 

 

Emerging Pompe Disease Drugs Under Different Phases of Clinical Development Include:

  • M 021: M6P Therapeutics
  • GYS1 Knockdown Oligonucleotide: Entrada Therapeutics
  • MZE 001: Maze Therapeutics
  • AT845: Astellas Gene Therapies
  • AAV2/8LSPhGAA: Asklepios Biopharmaceutical
  • SPK-3006: Spark Therapeutic
  • Cipaglucosidase alfa: Amicus Therapeutics 

 

Get a Free Sample PDF Report to know more about Pompe Disease Pipeline Assessment- https://www.delveinsight.com/sample-request/pompe-disease-pipeline-insight?utm_source=abnewswire&utm_medium=pressrelease&utm_campaign=gpr

 

Pompe Disease Pipeline Analysis:

The Pompe Disease pipeline report provides insights into 

  • The report provides detailed insights about companies that are developing therapies for the Pompe Disease treatment with aggregate therapies developed by each company for the same.
  • It accesses the Different therapeutic candidates segmented into early-stage, mid-stage, and late-stage of development for Pompe Disease Treatment.
  • Pompe Disease key companies are involved in targeted therapeutics development with respective active and inactive (dormant or discontinued) projects.
  • Pompe Disease Drugs under development based on the stage of development, route of administration, target receptor, monotherapy or combination therapy, a different mechanism of action, and molecular type. 
  • Detailed analysis of collaborations (company-company collaborations and company-academia collaborations), licensing agreement and financing details for future advancement of the Pompe Disease market.

The report is built using data and information traced from the researcher’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations, and featured press releases from company/university websites and industry-specific third-party sources, etc.

 

Further Pompe Disease product details are provided in the report. Download the Pompe Disease pipeline report to learn more about the emerging Pompe Disease therapies at: https://www.delveinsight.com/sample-request/pompe-disease-pipeline-insight?utm_source=abnewswire&utm_medium=pressrelease&utm_campaign=gpr

 

Pompe Disease Pipeline Market Drivers

  • Improving Healthcare Infrastructure
  • Demand for New and Effective Drugs
  • Increasing research and development in the gene therapy and enzyme replacement therapy areas

 

Pompe Disease Pipeline Market Barriers

  • Lack Of Cost-Effective Treatment

 

Scope of Pompe Disease Pipeline Drug Insight    

  • Coverage: Global
  • Key Pompe Disease Companies: M6P Therapeutics, Entrada Therapeutics, Maze Therapeutics, Astellas Gene Therapies, Asklepios Biopharmaceutical, Spark Therapeutic, Amicus Therapeutics, and others
  • Key Pompe Disease Therapies: M 021, GYS1 Knockdown Oligonucleotide, MZE 001, AT845, AAV2/8LSPhGAA, SPK-3006, Cipaglucosidase alfa, and others
  • Pompe Disease Therapeutic Assessment: Pompe Disease current marketed and Pompe Disease emerging therapies
  • Pompe Disease Market Dynamics: Pompe Disease market drivers and Pompe Disease market barriers 

 

Request for Sample PDF Report for Pompe Disease Pipeline Assessment and clinical trials- https://www.delveinsight.com/sample-request/pompe-disease-pipeline-insight?utm_source=abnewswire&utm_medium=pressrelease&utm_campaign=gpr

 

Table of Contents

1

Pompe Disease Report Introduction

2

Pompe Disease Executive Summary

3

Pompe Disease Overview

4

Pompe Disease- Analytical Perspective In-depth Commercial Assessment

5

Pompe Disease Pipeline Therapeutics

6

Pompe Disease Late Stage Products (Phase II/III)

7

Pompe Disease Mid Stage Products (Phase II)

8

Pompe Disease Early Stage Products (Phase I)

9

Pompe Disease Preclinical Stage Products

10

Pompe Disease Therapeutics Assessment

11

Pompe Disease Inactive Products

12

Company-University Collaborations (Licensing/Partnering) Analysis

13

Pompe Disease Key Companies

14

Pompe Disease Key Products

15

Pompe Disease Unmet Needs

16 

Pompe Disease Market Drivers and Barriers

17

Pompe Disease Future Perspectives and Conclusion

18

Pompe Disease Analyst Views

19

Appendix

20

About DelveInsight

 

Download Sample PDF Report to know more about Pompe Disease drugs and therapies-  https://www.delveinsight.com/sample-request/pompe-disease-pipeline-insight?utm_source=abnewswire&utm_medium=pressrelease&utm_campaign=gpr

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Company Name: DelveInsight Business Research LLP
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Email: Send Email
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Website: https://www.delveinsight.com

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